Forzinity

全球首款巴思综合征治疗药物

全球首款罕见病巴思综合征疗法：Elamipretide获FDA加速批准

Elamipretide（Forzinity）成为全球首个获FDA批准的巴思综合征疗法，为患者带来全新希望。本文回顾其意外发现、公司的研发历程、临床数据及监管挑战。

Forzinity

From Discovery to FDA Approval: Forzinity Becomes First Therapy for Barth Syndrome

Forzinity (elamipretide) makes history as the first FDA-approved therapy for Barth syndrome. Learn about Hazel Szeto’s discovery, Stealth Biotherapeutics’ development journey, and the clinical evidence supporting approval.